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    Academic Journals

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• Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice.

  Authors:Sam Hana, Michael Peterson, Helen McLaughlin, Eric Marshall, Attila J. Fabian, Olivia McKissick, et al.From:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20218,669 words Report 1500L

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• Schwann cell gene therapies in sight.

  Author:Stephan ZüchnerFrom:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20211,393 words Article 1530L

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• Gene therapy for spinal muscular atrophy: the Qatari experience.

  Authors:Hossamaldein Gaber Ali, Khalid Ibrahim, Mahmoud Fawzi Elsaid, Reem Babiker Mohamed, Mahmoud I. A. Abeidah, Azhar Othman Al Rawwas, et al.From:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20214,405 words Report 1420L

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• Correction to: Recent development of AAV-based gene therapies for inner ear disorders.

  Authors:Yiyang Lan, Yong Tao, Yunfeng Wang, Junzi Ke, Qiuxiang Yang, Xiaoyi Liu, et al.From:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 2021198 words Correction notice, B... 1410L

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• Knockdown of LINC00467 contributed to Axitinib sensitivity in hepatocellular carcinoma through miR-509-3p/PDGFRA axis.

  Authors:Wei Li, Yufeng He, Wei Chen, Wenling Man, Qiang Fu, Hongtong Tan, et al.From:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20216,062 words Report 1440L

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• Toward a new framework for the development of individualized therapies.

  Authors:Peter Marks and Celia WittenFrom:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20211,848 words Article 1810L

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• AAV9-mediated Schwann cell-targeted gene therapy rescues a model of demyelinating neuropathy.

  Authors:Alexia Kagiava, Christos Karaiskos, Jan Richter, Christina Tryfonos, Matthew J. Jennings, Amanda J. Heslegrave, et al.From:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 202112,475 words Report 1540L

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• Insights and future directions of potential genetic therapy for Apert syndrome: A systematic review.

  Authors:Nisreen Mohammed Al-Namnam, Soher Nagi Jayash, Firdaus Hariri, Zainal Ariff Abdul Rahman, and Mohammed Abdullah AlshawshFrom:Gene Therapy (Vol. 28, Issue 10-11) Peer-Reviewed

  Nov. 20218,175 words Report 1450L

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